Spinal muscular atrophy (SMA) is a severe neurological disease for which there is presently no cure, although current therapies can alleviate symptoms. In the search for better treatment options, ...

What is SMA? The rare genetic condition that Jesy Nelson’s twin daughters have - Former Little Mix star revealed her twin ...

Jesy Nelson's twin daughters Ocean Jade and Story Monroe have been diagnosed with spinal muscular atrophy (SMA) ...

Scotland has become the first UK nation to screen all newborn babies for spinal muscular atrophy. Here is what you need to ...

Patients with SMA often suffer from impaired bulbar function, which negatively affects quality of life and can be difficult to treat effectively. A German study prospectively followed children with ...

In a letter to European patients, Roche said its decision to end development of “emugrobart” was based on the drug “not ...

Please provide your email address to receive an email when new articles are posted on . Evrysdi is the only FDA-approved, noninvasive, disease-modifying treatment for spinal muscular atrophy. The ...

Scholar Rock contends its experimental drug for spinal muscular atrophy can achieve what none of the currently available therapies can do to treat this rare disease. After positive data from a pivotal ...