Follow TNM’s WhatsApp channel for news updates and story links.L Muruganatham, a disability rights activist and lawyer in the ...

Sevasemten is an investigational agent that is currently not approved for use by any regulatory authority in any ...

IBEC researcher Juanma Fernández recently has received funding from the French AFM-Telethon to carry out the project “Monitoring of fibrotic processes in 3D skeletal muscle co-cultures for Muscular ...

Parents of boys with Duchenne muscular dystrophy weigh in on drug innovation and medical regulation.

An alternative to using standard glucocorticoids is the synthetic dissociative steroid vamorolone (Agamree), which was ...

The FDA has reported that the recent death of an 8-year-old boy was unrelated to Sarepta Therapeutics’ gene therapy Elevidys and recommended lifting the voluntary hold on the treatment, which is used ...

The FDA is investigating the death of an 8-year-old boy who received Elevidys, a gene therapy developed by Sarepta Therapeutics to treat Duchenne muscular dystrophy. The child died June 7, prompting ...

A new investigation into Duchenne muscular dystrophy (DMD) pathogenesis suggests that at least part of the muscle degeneration observed in DMD patients may result from the reduced production of ...

After our editorial, the agency relents to allow a Duchenne treatment.

Nur, an expert in regenerative and muscle biology. However, he hasn't yet tasted the cultivated meat because human ...