An alternative to using standard glucocorticoids is the synthetic dissociative steroid vamorolone (Agamree), which was ...

Parents of boys with Duchenne muscular dystrophy weigh in on drug innovation and medical regulation.

Sevasemten is an investigational agent that is currently not approved for use by any regulatory authority in any ...

IBEC researcher Juanma Fernández recently has received funding from the French AFM-Telethon to carry out the project “Monitoring of fibrotic processes in 3D skeletal muscle co-cultures for Muscular ...

Nur, an expert in regenerative and muscle biology. However, he hasn't yet tasted the cultivated meat because human ...

The FDA has reported that the recent death of an 8-year-old boy was unrelated to Sarepta Therapeutics’ gene therapy Elevidys and recommended lifting the voluntary hold on the treatment, which is used ...

Roche has halted some international shipments of the gene therapy Elevidys, used to treat Duchenne muscular dystrophy, Bloomberg reported July 22. The decision comes in the wake of a similar move by ...

MicroRNA-33a and microRNA-33b are encoded within the mammalian SREBF1 and SRBF2 genes, respectively, and both SREBF1 and ...

Sarepta Therapeutics is pausing shipments of its gene therapy for muscular dystrophy following several patient deaths that ...

On Sunday, a local family held their fourth annual Cornhole for a Cure fundraiser, raising money for the Muscular Dystrophy ...

Columnist Patrick Moeschen emphasizes the importance of making advance directives and shares some tips for how to get started ...

The Supreme Court held that denial of reasonable accommodation in custody violates Articles 14 and 21 of the Constitution and breaches the RPwD Act, 2016 ...